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  4. RegenMedEd Webinar: The Critical Role of Patients in Advancing Gene Therapy Treatments for Rare Diseases - 03/09/2022
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Workshop

Event Title
RegenMedEd Webinar: The Critical Role of Patients in Advancing Gene Therapy Treatments for Rare Diseases
March 9, 2022

Date:
March 9, 2022
Time:
11:00 AM - 12:00 PM ET
Organized By:
Organizer

The FDA’s Center for Biologics Evaluation and Research (CBER) Office of Tissues and Advanced Therapies (OTAT) is hosting a public webinar on Wednesday, March 9, 2022, from 11:00 a.m. - 12:00 p.m. ET. 

The webinar, The Critical Role of Patients in Advancing Gene Therapy Treatments for Rare Diseases, will bring together patients, caregivers, advocates, and other important stakeholders to celebrate and recognize the contributions that patients with rare diseases have made to advancements in regenerative medicine. This event follows Rare Disease Day, an international day for awareness of rare diseases.

There are around 7,000 known rare diseases affecting more than 30 million people in the United States. Many rare diseases are life-threatening, and only a fraction of rare diseases have an available treatment. The FDA remains committed to supporting the development of treatments for rare diseases and engaging with the rare disease community.

Infocard sharing various images of people and patients.

About the Webinar

The webinar will feature panelists to discuss:

  • Perspectives from patients living with a rare disease and their experiences participating in clinical research
  • Ways patients and caregivers can participate in and advance clinical research for rare diseases
  • Why and how regenerative medicine may hold promise for patients with rare diseases
  • FDA’s efforts and programs to support the development of rare disease treatments, including regenerative medicine like gene and cell therapies

This webinar is the second in an educational webinar series called RegenMedEd: An FDA CBER OTAT Webinar Series on Regenerative Medicine. 

Registration is required. Please register for the webinar now.

Meeting Information & Registration

  • Date: Wednesday, March 9
  • Time: 11:00 a.m.–12:00 p.m. ET
  • Location: The webinar will be held via Zoom.
  • Registration: Registration is required to attend the webinar. Please register for the webinar now. 
  • Get Involved: Use the hashtag #RegenMedEd on Twitter to share a question with the panelists in advance!

What is Regenerative Medicine?

Regenerative medicine therapies, such as cell and gene therapies, hold promise for transforming medicine and creating options for patients living with difficult, rare, and often incurable diseases. The FDA plays a vital role in facilitating the development of regenerative medicine therapies, as well as in ensuring approved products are safe and effective for patients.

About the RegenMedEd Webinar Series

To further engage patients, caregivers, and advocates on the topic of regenerative medicine, OTAT launched an educational webinar series called RegenMedEd: An FDA CBER OTAT Webinar Series on Regenerate Medicine. The RegenMedEd webinar series aims to bring together patients, caregivers, patient advocates, and FDA staff to discuss foundational information about regenerative medicine therapies, such as gene therapy and cell therapy, and explore opportunities for stakeholders to engage with the FDA to help advance drug development.

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